New gene therapies may soon treat dozens of rare diseases, but expense may limit availability for many
Zolgensma—which treats spinal muscular atrophy, a rare genetic disease that damages nerve cells, l...
Animal model opens way to test Alzheimer’s disease therapies
Our knowledge of Alzheimer’s disease has gro...
Research uncovers new potential target for ovarian cancer therapies
Promoting gamma delta T cell response could be an ...
Nuclear magnetic resonance insights set stage for next-gen targeted cancer therapies for adults and children
Scientists at St. Jude Children’s Research H...
New study takes aim at advanced types of non-addictive pain therapies
A team of scientists from ASU’s School of Mo...
Sanfilippo C syndrome: New brain cell models to evaluate therapies
The Sanfilippo syndrome type C is a severe neurode...
Releasing brakes: Potential new methods for Duchenne muscular dystrophy therapies
Researchers identified a group of small molecules ...